Key Players
- Ascendis Pharma A/S
- BioMarin Pharmaceutical Inc
- Eli Lilly and Company
- Ipsen S.A
- Novartis
- Novo Nordisk A/S
- OPKO Health
- Orphan Biovitrum AB
- The Vanguard Group
- Sanofi Genzyme
- Takeda Pharmaceutical Company Limited
- Ultragenyx Pharmaceutical Inc