Key Players
- Abeona Therapeutics Inc
- Bio Marin Pharmaceutical Inc
- BioMarin Pharmaceutical Inc
- Denali Therapeutics Inc
- Greenovation Biotech GmbH
- JCR Pharmaceuticals Co. Ltd
- Lysogene S.A
- Orphazyme A/S
- Passage Bio, inc
- Prevail Therapeutics
- REGENXBIO Inc
- Sanofi Genzyme
- Takeda Pharmaceutical Company Limited
- ULTRAGENE PHARMA INC
- Ultragenyx Pharmaceutical Inc
