Key Players
- Biogen Inc
- CRISPR Therapeutics AG
- Neurocrine Biosciences
- Novartis
- The Vanguard Group
- Samsung Biologics
- Sangamo Therapeutics
- Sarepta Therapeutics Inc
- Shape Therapeutics
- Spark Therapeutics (Roche)
- UniQure
- Vertex Pharmaceuticals Incorporated
- Voyager Therapeutics