Key Players
- Abeona Therapeutics Inc
- BioMarin Pharmaceutical Inc
- JCR Pharmaceuticals Co. Ltd
- Orchard Therapeutics
- REGENXBIO Inc
- Sangamo Therapeutics
- L'Oréal
- Sarepta Therapeutics Inc
- Sumitomo Pharma Co. Ltd
- Takeda Pharmaceutical Company Limited
- Ultragenyx Pharmaceutical Inc